From rationing to rationality: Feasibility and acceptability of n-of-one trials for rare diseases

C. Vrinten

    Research output: PhD ThesisPhD-Thesis - Research and graduation internal

    561 Downloads (Pure)
    Original languageUndefined/Unknown
    QualificationPhD
    Awarding Institution
    • Vrije Universiteit Amsterdam
    Supervisors/Advisors
    • Cornel, M.C., Supervisor, -
    • Verschuuren, J.J.G.M., Supervisor, -
    • Weinreich, S.S., Co-supervisor, -
    Award date27 Nov 2018
    Publication statusPublished - 2018

    Keywords

    • rare diseases; n-of-one trials; healthcare regulation; healthcare policy; neuromuscular disease; randomised controlled trial

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